Ultragenyx Pharmaceutical Inc.
Ultragenyx Pharmaceutical Inc.
RARE
Valuace
70
Růst
0
Zdraví
75
Cena
$ 30.45
Dnes
--1.01 (-4.30%)
Souhrn
Výkazy
Ukazatele
Profil
Držitelé
Návštěvnost webu
Konkurence
Zprávy společnosti
Kapitalizace
2.9B
Obrat
1B
Zisk
-1B
Aktiva
1B
Dluh
1B
ROE
0%
ROA
0%
PE
-3
PS
3
Cena 1R
18-47
⌀ Cena
32.42
Dividenda
0.0(0.0%)
Čtvrtletní 10-Q
10-Q
Celoroční 10-K
8-K
Nadcházející oznámení zisků
12-02-2026
Poslední dividenda

Profil

Společnost Ultragenyx Pharmaceutical Inc., biofarmaceutická společnost, se zaměřuje na identifikaci, získání, vývoj a komercializaci nových produktů pro léčbu vzácných a ultravzácných genetických onemocnění v Severní Americe, Evropě a mezinárodně. Mezi jeho biologické produkty patří Crysvita (burosumab), protilátka cílící na fibroblastový růstový faktor 23 pro léčbu hypofosfatémie vázané na X, stejně jako osteomalacie vyvolaná nádorem; Mepsevii, enzymová substituční terapie pro léčbu dětí a dospělých s mukopolysacharidózou VII; Dojolvi pro léčbu oxidačních poruch mastných kyselin s dlouhým řetězcem; a Evkeeza (evinacumab) pro léčbu homozygotní familiární hypercholesterolemie. Kandidatury produktů společnosti zahrnují DTX401, adenem asociovaný virus 8 (AAV8), genovou terapii klinického kandidáta pro léčbu pacientů s glykogenní paměťovou chorobou typu Ia; DTX301, genovou terapii AAV8 pro léčbu pacientů s ornitin-transkarbamylázou; UX143, lidskou monoklonální protilátku pro léčbu osteogenesis imperfecta; GTX-102, antisense oligonukleotid pro léčbu Angelmanova syndromu; UX701, pro léčbu Wilsonovy choroby; a UX053 pro léčbu glykogenové paměťové choroby typu III. Společnost Ultragenyx Pharmaceutical Inc. spolupracuje a má licenční smlouvu s Kyowa Kirin Co., Ltd.; Univerzita Saint Louis; Baylor Research Institute; REGENXBIO Inc.; Bayer Healthcare LLC; GeneTx; Mereo; Pennsylvania; Arcturus Therapeutics Holdings Inc., Solid Biosciences Inc.; a Daiichi Sankyo Co., Ltd. Společnost Ultragenyx Pharmaceutical Inc. byla založena v roce 2010 a sídlí v Novatu v Kalifornii.
Sektor
Healthcare
Odvětví
Biotechnology
Počet zaměstnanců
1294
Založení
2014-01-31
Adresa
60 Leveroni Court
CEO
Emil D. Kakkis

Zahraniční články

Výsledovka

Rozvaha

Peněžní toky

Výsledovka

Výsledovka
Rozvaha
Peněžní toky
V miliónech (USD)
Revenue TTM 202520242023202220212020201920182017201620152014201320122011
Total Revenues672.7673.0560.2434.2363.3351.4271.0103.751.52.60.10.00.00.00.00.0
Cost of Revenues108.7109.076.745.228.316.06.19.01.10.00.00.00.00.00.00.0
Gross Profit564.1564.0483.5389.0335.0335.4264.994.750.32.60.10.00.00.00.00.0
Revenue 4-20253-20252-20251-20254-20243-20242-20241-20244-20233-2023
Total Revenues207.0159.9166.5139.3164.9139.5147.0108.8127.498.1
Cost of Revenues29.028.023.028.716.921.021.317.512.111.0
Gross Profit178.0131.9143.5110.6148.0118.5125.791.3115.387.1
Operating Income TTM 202520242023202220212020201920182017201620152014201320122011
R&D Expenses0.00.00.0648.4705.8497.2412.1357.4294.0231.6183.2114.746.027.812.64.7
Selling General & Admin Expenses0.00.00.0309.8278.1220.0182.9161.5127.799.964.933.010.84.53.31.8
Depreciation & Amortization35.035.035.526.09.50.27.612.519.55.83.41.40.70.40.30.0
Total Operating Expenses1,099.81,099.01,019.5958.2983.9717.1595.0518.9421.7331.6248.1147.756.832.316.06.6
Operating Income-535.7-535.0-536.0-569.2-648.9-381.7-330.1-424.2-371.4-328.9-248.0-147.7-56.8-32.3-16.0-6.6
Operating Income TTM 4-20253-20252-20251-20254-20243-20242-20241-20244-20233-2023
R&D Expenses0.00.00.00.00.00.00.00.0160.6157.2
Selling General & Admin Expenses0.00.00.00.00.00.00.00.076.874.9
Depreciation & Amortization8.88.68.69.09.18.88.98.88.27.2
Total Operating Expenses292.0302.8251.4253.6270.3250.5242.1256.6237.4232.2
Operating Income-114.0-170.9-107.9-142.9-122.3-132.0-116.4-165.3-122.0-145.1
Net Income TTM 202520242023202220212020201920182017201620152014201320122011
Interest Income25.025.036.526.711.11.97.013.29.54.13.82.30.60.20.00.0
Interest Expense61.562.063.066.043.029.433.31.10.00.00.00.00.00.00.00.3
Other Expense-35.6-36.0-31.6-39.3-52.8-71.2144.824.7174.310.62.2-0.2-3.0-3.0-0.40.0
IBT-571.3-571.0-567.6-608.5-701.7-453.0-185.4-399.4-197.1-318.3-245.8-145.6-59.8-35.1-16.3-6.8
Income Tax Expense4.14.01.6-1.85.71.01.23.30.5-16.20.0-2.3-0.7-3.0-0.40.2
Net Income-575.4-575.0-569.2-606.6-707.4-454.0-186.6-402.7-197.6-302.1-245.9-145.6-59.8-35.1-16.3-6.8
Net Income TTM 4-20253-20252-20251-20254-20243-20242-20241-20244-20233-2023
Interest Income6.55.95.86.89.610.77.48.88.65.9
Interest Expense19.014.114.014.315.515.716.015.817.317.7
Other Expense-14.0-8.7-6.1-6.8-11.1-1.2-14.4-4.9-4.8-13.9
IBT-128.0-179.5-114.0-149.8-133.4-133.2-130.7-170.2-126.9-159.0
Income Tax Expense1.00.90.91.30.00.30.90.5-3.70.7
Net Income-129.0-180.4-115.0-151.1-133.4-133.5-131.6-170.7-123.2-159.6
Per Share Data TTM 202520242023202220212020201920182017201620152014201320122011
EPS$0.00$0.00$0.00$-8.25$-10.12$-6.70$-3.07$-7.12$-3.97$-7.12$-6.21$-3.96$-2.08$-1.21$-0.71$-0.30
EPS Diluted$0.00$0.00$0.00$-8.25$-10.12$-6.70$-3.07$-7.12$-3.97$-7.12$-6.21$-3.96$-2.08$-1.21$-0.71$-0.30
Shares Outstanding99.998.690.573.569.967.860.856.649.842.539.636.828.829.123.123.1
Diluted Shares Outstanding99.998.690.573.569.967.860.856.649.842.539.636.828.829.123.123.1
Per Share Data TTM 4-20253-20252-20251-20254-20243-20242-20241-20244-20233-2023
EPS$0.00$0.00$0.00$0.00$0.00$0.00$0.00$0.00$-1.52$-2.23
EPS Diluted$0.00$0.00$0.00$0.00$0.00$0.00$0.00$0.00$-1.52$-2.23
Shares Outstanding99.999.898.596.395.795.586.684.381.171.7
Diluted Shares Outstanding99.999.898.596.395.795.586.684.381.171.7
Current Assets TTM 20242023202220212020201920182017201620152014201320122011
Cash And Equivalents486.9173.7213.6132.9307.6713.5433.6113.4100.5161.193.624.37.486.210.6
Short Term Investments283.1436.3363.6614.8432.6488.0321.6346.3134.0219.0343.4163.246.00.00.0
Total Cash & ST Investments770.0610.0577.2896.7999.11,212.0760.4459.7244.5498.1437.0187.553.486.210.6
Accounts Receivable108.3121.873.440.428.423.132.812.75.20.00.00.00.00.00.1
Inventory40.145.034.026.816.213.011.57.10.80.00.00.00.00.00.0
Other Current Assets46.240.347.668.9-187.247.146.242.929.221.513.25.91.80.30.2
Total Current Assets964.6817.1732.2883.9856.61,295.3851.0522.4244.5498.1450.2187.555.286.411.0
Current Assets 3-20252-20251-20254-20243-20242-20241-20244-20233-20232-2023
Cash And Equivalents202.5166.1127.1173.7150.6480.7112.3213.672.6102.1
Short Term Investments222.7311.3367.4436.3471.0283.1299.8363.6369.5449.9
Total Cash & ST Investments425.2477.4494.4610.0621.6763.8412.1777.1524.2552.0
Accounts Receivable112.5124.598.8121.893.3106.0100.373.479.370.5
Inventory52.246.546.045.043.340.135.934.031.828.3
Other Current Assets53.271.459.840.341.454.747.747.646.051.4
Total Current Assets643.2719.8699.2817.1799.6964.6596.0732.2524.2702.1
Long-Term Assets TTM 20242023202220212020201920182017201620152014201320122011
Net Property, Plant & Equipment278.7265.9290.6285.7176.2114.074.720.021.817.17.43.01.31.40.8
Goodwill44.444.444.444.444.444.444.444.444.40.00.00.00.00.00.0
Intangible Assets166.2178.3166.3160.1130.8131.1129.0129.2141.50.00.00.00.00.00.0
Long-Term Investments114.1135.0199.9154.5293.9165.932.90.010.0118.099.30.00.00.00.0
Other Long-Term Assets50.462.757.716.820.68.83.53.53.4-92.52.77.43.10.50.4
Total Long-Term Assets653.8686.3758.8661.5665.8464.3284.5197.2246.342.5109.410.54.41.91.2
Total Assets1,618.41,503.51,491.01,545.41,522.41,759.61,135.5719.6490.8540.6559.6198.059.688.312.1
Long-Term Assets 3-20252-20251-20254-20243-20242-20241-20244-20233-20232-2023
Net Property, Plant & Equipment250.0255.8260.9265.9272.4278.7285.1290.6323.2308.2
Goodwill44.444.444.444.444.444.444.444.444.444.4
Intangible Assets172.9174.7176.5178.3164.9166.2165.0166.3157.3158.2
Long-Term Investments22.151.568.6135.0203.1110.7156.6199.94.071.8
Other Long-Term Assets57.960.162.462.753.953.860.051.7110.026.5
Total Long-Term Assets547.2586.5612.8686.3738.8653.8711.1758.8714.0609.2
Total Assets1,190.41,306.31,311.91,503.51,538.41,618.41,307.11,491.01,238.11,311.3
Current Liabilities TTM 20242023202220212020201920182017201620152014201320122011
Accounts Payable59.838.842.143.317.112.912.912.38.95.42.94.91.41.20.3
Short-Term Debt58.610.312.611.811.19.07.20.00.00.00.00.00.00.00.0
Other Current Liabilities154.4295.1225.7204.7145.6108.583.262.556.154.925.07.74.52.00.7
Current Liabilities272.9344.2280.4261.2181.4189.6103.374.771.060.327.912.55.93.21.0
Current Liabilities 3-20252-20251-20254-20243-20242-20241-20244-20233-20232-2023
Accounts Payable40.634.247.538.836.059.841.042.133.442.1
Short-Term Debt77.711.810.510.310.411.712.812.612.110.9
Other Current Liabilities221.8247.2233.7295.1238.6201.3191.8225.7208.6191.4
Current Liabilities340.0293.2291.7344.2285.0272.9245.6280.4254.0244.4
Long-Term Liabilities TTM 20242023202220212020201920182017201620152014201320122011
Long-Term Debt842.230.030.619.830.939.329.80.00.00.00.00.00.00.00.0
Capital Leases25.740.343.231.642.048.237.00.00.00.00.00.00.00.00.0
Def. Tax Liability30.130.130.131.733.333.333.331.231.20.00.00.00.00.00.0
Total Liabilities1,186.01,241.21,215.61,193.0599.8605.2481.7110.7107.366.728.513.09.54.01.5
Long-Term Liabilities 3-20252-20251-20254-20243-20242-20241-20244-20233-20232-2023
Long-Term Debt785.424.527.830.023.725.728.030.634.614.8
Capital Leases33.836.338.340.334.137.540.843.212.125.7
Def. Tax Liability0.030.130.130.130.130.130.130.131.731.7
Total Liabilities1,174.31,148.01,160.71,241.21,184.51,186.01,166.81,215.61,206.41,182.3
Total Common Equity TTM 20242023202220212020201920182017201620152014201320122011
Common Stock0.10.10.10.10.10.10.10.10.00.00.00.00.00.00.0
Retained Earnings-3,689.9-3,956.8-3,387.7-2,781.0-2,073.6-1,619.6-1,433.0-1,030.3-832.7-530.5-284.7-139.0-74.8-27.1-8.2
Comprehensive Income2.3-0.60.6-6.6-1.40.7-0.1-0.6-5.70.9-0.9-0.20.0-0.40.0
Total Common Equity432.4255.3275.4352.5922.61,154.4653.8608.9383.5474.0531.1184.950.184.310.6
Total Common Equity 3-20252-20251-20254-20243-20242-20241-20244-20233-20232-2023
Common Stock0.10.10.10.10.10.10.10.10.10.1
Retained Earnings-4,403.3-4,222.9-4,107.9-3,956.8-3,823.5-3,689.9-3,558.3-3,387.7-3,264.5-3,104.8
Comprehensive Income8.8-0.3-0.3-0.60.9-1.1-0.40.6-2.2-3.1
Total Common Equity9.2151.3144.2255.3346.8432.4140.3275.431.7129.0
Other TTM 20242023202220212020201920182017201620152014201320122011
Total Debt926.540.343.231.642.048.237.00.00.00.00.00.00.00.00.0
Book Value432.4262.3275.4352.5922.61,154.4653.8608.9383.5474.0531.1184.950.184.310.6
Other 3-20252-20251-20254-20243-20242-20241-20244-20233-20232-2023
Total Debt7.07.07.07.07.00.00.00.00.00.0
Book Value9.2151.3144.2255.3346.8432.4140.3275.431.7129.0
Cash Flow From Operating Activities TTM 202520242023202220212020201920182017201620152014201320122011
Net Income-585.1-575.0-569.2-606.6-707.4-454.0-186.6-402.7-197.6-302.1-245.9-145.6-59.8-35.1-16.3-6.8
Depreciation & Amortization33.10.035.526.018.213.212.38.519.55.83.41.40.70.40.30.0
Stock-Based Compensation144.9153.0158.0135.2130.4105.085.782.080.168.048.324.95.40.70.90.3
Change Working Capital-23.6-23.013.9-15.160.2-63.2104.7-15.9-24.8-20.226.37.72.2-1.52.30.5
Change In Accounts Receivable-27.9-31.0-33.6-22.8-12.1-5.49.8-20.1-7.60.00.00.00.00.00.00.0
Change In Accounts Payable13.124.047.02.487.42.829.620.63.43.52.5-2.03.20.20.90.3
Change In Inventories-11.7-6.0-11.2-6.9-9.7-3.1-1.3-4.5-5.30.00.00.00.00.00.00.0
Other Non-cash Items252.5-21.0-52.5-12.7119.811.721.51.7-0.210.90.75.66.94.30.30.3
Cash from Operations-469.50.00.0-474.8-380.5-338.7-132.2-345.4-290.6-253.8-161.0-106.0-44.6-31.2-12.5-5.8
Cash Flow From Operating Activities 4-20253-20252-20251-20254-20243-20242-20241-20244-20233-2023
Net Income-129.0-180.4-115.0-151.1-133.4-133.5-131.6-170.7-123.2-159.6
Depreciation & Amortization0.08.6-11.89.09.18.88.98.88.27.2
Stock-Based Compensation38.037.038.539.940.241.639.436.933.734.9
Change Working Capital0.654.9-21.8-56.622.830.816.4-56.013.32.8
Change In Accounts Receivable-33.85.4-12.710.1-20.69.82.2-24.91.0-6.2
Change In Accounts Payable37.045.1-9.7-48.50.00.025.3-35.515.97.5
Change In Inventories0.2-5.60.2-0.8-2.5-2.5-4.1-2.1-2.0-3.5
Other Non-cash Items-9.4-11.51.7-7.7-18.1-14.6-10.0-9.8123.2-1.8
Cash from Operations0.00.00.00.00.00.00.00.0-83.9-117.9
Cash Flow From Investing Activities TTM 202520242023202220212020201920182017201620152014201320122011
Capital Expenditure-23.00.0-7.5-44.3-146.1-73.1-43.9-24.8-4.1-2.8-10.2-5.0-2.1-0.4-1.1-0.5
Acquisitions2.50.00.00.0-75.00.00.00.00.0-142.80.00.00.00.00.00.0
Investments-386.40.0-408.6-526.4-614.7-1,012.2-850.3-707.2-509.8-230.5-442.5-624.2-209.0-64.00.00.0
Sales of Investment524.50.0413.3746.2545.1890.9720.6719.0310.2431.6543.8338.488.016.60.00.0
Other Investing Activities-2.80.00.0-7.5-0.8-0.9-5.60.0170.30.9-1.2-1.5-0.30.0-0.1-0.4
Cash from Investing112.30.00.0168.0-291.7-195.4-179.1-13.0-33.356.489.9-292.4-123.4-47.7-1.2-0.9
Cash Flow From Investing Activities 4-20253-20252-20251-20254-20243-20242-20241-20244-20233-2023
Capital Expenditure0.0-1.3-2.5-1.3-0.7-1.6-2.0-3.2-1.6-3.7
Acquisitions0.00.00.00.00.00.00.00.02.50.0
Investments0.00.0-15.50.0-15.9-367.4-3.4-21.9-221.6-139.5
Sales of Investment0.00.089.4137.0119.493.768.5131.6116.4207.9
Other Investing Activities0.00.00.00.00.00.00.00.0-0.3-0.4
Cash from Investing0.00.00.00.00.00.00.00.0-107.064.3
Cash Flow From Financing Activities TTM 202520242023202220212020201920182017201620152014201320122011
Debt Repaid0.00.00.00.00.00.00.00.00.0-4.90.00.00.00.00.00.0
Debt Issued900.840.3-2.811.6-10.4-6.311.237.00.04.90.00.00.00.00.00.0
Issuance of Common Stock769.20.00.0379.810.878.9511.2355.2309.0132.079.5467.6189.30.20.10.0
Repurchase of Common Stock0.00.00.00.00.00.00.00.00.00.00.00.00.00.00.00.0
Dividends Paid0.00.00.00.00.00.00.00.00.00.00.00.0-4.30.00.00.0
Other Financing Activities740.70.00.08.4490.439.689.1324.127.89.359.20.00.00.089.117.3
Cash from Financing740.70.00.0388.1501.2118.6600.3679.3336.9136.3138.7467.6185.00.289.217.3
Cash Flow From Financing Activities 4-20253-20252-20251-20254-20243-20242-20241-20244-20233-2023
Debt Repaid0.00.00.00.00.00.00.00.00.00.0
Debt Issued863.1826.8-2.0-2.16.3-3.4-3.3-2.431.1-13.7
Issuance of Common Stock0.00.00.00.00.00.00.00.0326.524.8
Repurchase of Common Stock0.00.00.00.00.00.00.00.00.00.0
Dividends Paid0.00.00.00.00.00.00.00.00.00.0
Other Financing Activities0.00.00.00.00.00.00.00.04.20.4
Cash from Financing0.00.00.00.00.00.00.00.0330.625.2
Cash position TTM 202520242023202220212020201920182017201620152014201320122011
Net Change in Cash387.1253.5-35.281.8-172.0-416.7290.1320.712.5-60.667.669.216.9-78.875.510.6
Closing Cash Balance486.9436.0184.2219.4137.6309.6726.3436.2115.5100.5161.193.624.37.486.210.6
Cash position 4-20253-20252-20251-20254-20243-20242-20241-20244-20233-2023
Net Change in Cash221.726.149.5-45.023.9-330.0367.9-97.0144.8-29.1
Closing Cash Balance436.0214.7188.6139.2184.2160.2490.3122.4219.478.6
Free Cash Flow TTM 202520242023202220212020201920182017201620152014201320122011
Free Cash Flow-492.5-472.0-421.7-521.6-526.6-411.8-176.1-370.2-294.6-256.6-171.2-110.9-46.8-31.6-13.6-6.4
Real Free Cash Flow-637.4-625.0-579.7-656.8-657.0-516.7-261.9-452.2-374.7-324.7-219.5-135.8-52.2-32.3-14.5-6.6
Free Cash Flow 4-20253-20252-20251-20254-20243-20242-20241-20244-20233-2023
Free Cash Flow-100.8-92.7-95.7-182.8-80.2-68.6-81.5-203.9-85.5-121.6
Real Free Cash Flow-138.8-129.7-134.3-222.7-120.3-110.2-120.8-240.9-119.2-156.4
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Ukazatel Aktuální Historické Konkurence
P/E-3.4-15-1.4
P/S35401.99.4
P/B122.813.95.2
P/FCF-3.2-14.1-1.5
Market cap$2.9$3.5
P/E (Price to Earnings Ratio) – Poměr ceny akcie k zisku za posledních 12 měsíců. Říká, kolik korun investor zaplatí za 1 korunu zisku. Např.: P/E = 15 znamená, že pokud akcie stojí 15 Kč, firma vydělala 1 Kč za poslední rok.

Finance

Ukazatel Aktuální Historické Srovnání
Debt to Assets0 %6.3 %0 %
Debt to Income-150 %-16 %0 %
Debt to Free cash flow-138 %-672.1 %0 %
Interest expense percentage-11.5 %-4.1 %44.7 %
Current ratio1.9 8.2 0

Efektivita

Ukazatel Aktuální Historické Srovnání
ROE-6282.8 %-245.7 %0 %
ROA-48.3 %-33.5 %0 %
CapEx to Revenue0.8 %1710 %0 %
RaD to Revenue0 %31302 %0 %
ROEM519,877.1 102986.4

Marže

Ukazatel Aktuální Historické Srovnání
Gross margin83.8 %68.9 %68.7 %
Operating margin-79.6 %-41665.5 %35.5 %
Net margin-85.5 %-40838.7 %9.5 %

Dividenda

Ukazatel Aktuální Historické Srovnání
Dividend yield0 %0 %0 %
Dividend payout percentage0 %-0.7 %0 %
Dividend yield (Dividendový výnos) ukazuje aktuální procentuální výnos z dividend vůči ceně akcie.

Ostatní

Ukazatel Aktuální Historické
Shares outstanding99.9 mil 55.3 mil
Employee count1.3 tis 0.7 tis

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